JAMA Neurology,
Approving a Problematic Muscular Dystrophy Drug: Implications for FDA Policy This Viewpoint discusses controversies surrounding…
Approving a Problematic Muscular Dystrophy Drug: Implications for FDA Policy This Viewpoint discusses controversies surrounding…
Approving a Problematic Muscular Dystrophy Drug: Implications for FDA Policy This Viewpoint discusses controversies surrounding…
Approving a Problematic Muscular Dystrophy Drug: Implications for FDA Policy This Viewpoint discusses controversies surrounding…
Approving a Problematic Muscular Dystrophy Drug: Implications for FDA Policy This Viewpoint discusses controversies surrounding…
Approving a Problematic Muscular Dystrophy Drug: Implications for FDA Policy This Viewpoint discusses controversies surrounding…
Approving a Problematic Muscular Dystrophy Drug: Implications for FDA Policy This Viewpoint discusses controversies surrounding…
Patients with Duchenne muscular dystrophy (DMD), need better treatments, and drugs like eteplirsen might... Patients with…